Accomplished RNA therapeutics leader with track record of advancing novel genetic medicines from discovery to FDA approval to ...

Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.

Genetic disorders occur due to alterations in the primary genetic material, deoxyribonucleic acid (DNA), of an organism.

A research team led by Associate Professor Hirofumi Nishizono and graduate student Masaki Kato from the Research Support ...

Therapeutic Potential of CRISPR–Cas3 Genome-Editing System for Transthyretin Amyloidosis. Credit: Institute of Medical ...

Learn more about whether Perrigo Company plc or Wave Life Sciences Ltd. is a better investment based on AAII's A+ Investor grades, which compare both companies' key financial metrics.

Wave expects to initiate a Phase 2a multidose portion of WVE-007 INLIGHT clinical trial in individuals living with obesity with higher BMI and ...

Scientists are testing CRISPR gene editing as a potential HIV cure after successfully removing the virus from infected cells ...

Gene-editing technologies show great promise for medical treatments and research, with the potential to cure thousands of ...

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...

Although the year brought a steady stream of new treatments, tests, and cutting-edge science, experts worry about how ...

Scientists have discovered a new CRISPR mechanism with precise activity, expanding the potential applications of the existing ...